TY - JOUR
AU - Narayanan, Dilip
AU - Tran, Kim T.
AU - Pallesen, Jakob S.
AU - Solbak, Sara M. Ø.
AU - Qin, Yuting
AU - Mukminova, Elina
AU - Luchini, Martina
AU - Vasilyeva, Kristina O.
AU - González Chichón, Dorleta
AU - Goutsiou, Georgia
AU - Poulsen, Cecilie
AU - Haapanen, Nanna
AU - Popowicz, Grzegorz M.
AU - Sattler, Michael
AU - Olagnier, David
AU - Gajhede, Michael
AU - Bach, Anders
TI - Development of Noncovalent Small-Molecule Keap1-Nrf2 Inhibitors by Fragment-Based Drug Discovery
JO - Journal of medicinal chemistry
VL - 65
IS - 21
SN - 0022-2623
CY - Washington, DC
PB - ACS
M1 - PUBDB-2022-06371
SP - 14481 - 14526
PY - 2022
N1 - Waiting for fulltext
AB - Targeting the protein–protein interaction (PPI) between the transcription factor nuclear factor erythroid 2-related factor 2 (Nrf2) and its repressor, Kelch-like ECH-associated protein 1 (Keap1), constitutes a promising strategy for treating diseases involving oxidative stress and inflammation. Here, a fragment-based drug discovery (FBDD) campaign resulted in novel, high-affinity (K<sub>i</sub> = 280 nM), and cell-active noncovalent small-molecule Keap1-Nrf2 PPI inhibitors. We screened 2500 fragments using orthogonal assays─fluorescence polarization (FP), thermal shift assay (TSA), and surface plasmon resonance (SPR)─and validated the hits by saturation transfer difference (STD) NMR, leading to 28 high-priority hits. Thirteen co-structures showed fragments binding mainly in the P4 and P5 subpockets of Keap1’s Kelch domain, and three fluorenone-based fragments featuring a novel binding mode were optimized by structure-based drug discovery. We thereby disclose several fragment hits, including their binding modes, and show how FBDD can be performed to find new small-molecule Keap1-Nrf2 PPI inhibitors.
LB - PUB:(DE-HGF)16
C6 - pmid:36263945
UR - <Go to ISI:>//WOS:000885322600001
DO - DOI:10.1021/acs.jmedchem.2c00830
UR - https://bib-pubdb1.desy.de/record/484604
ER -